Présentation
Publications scientifiques
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2026
Enhanced γ-globin reactivation and sickle cell correction through a repressor..., Mol Ther Nucleic Acids
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2025
Base editing of β-thalassemia mutations as a therapeutic strategy for severe ..., Sci Transl Med
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2025
Dissecting the epigenetic regulation of the fetal hemoglobin genes to unravel..., Nucleic Acids Res
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2023
Novel lentiviral vectors for gene therapy of sickle cell disease combining ge..., Mol Ther Nucleic Acids